Patrick and Amy sit down to hear her story—how she first got involved in the bleeding disorders community back in 2003, and how patient advocacy became her passion. Along the way, they share laughs about their unexpected pasts as actors and the moments that shaped their paths.

Also on this episode of BloodStream, our hosts also look back on the year in gene therapy, spotlighting patients, clinicians, and researchers who are redefining what’s possible, including five-year insights from the HOPE-B study in hemophilia B.

This episode is a celebration of hope, trust, and progress—a reminder that hemophilia care isn’t just about science, it’s about people and the possibilities they create.

Presenting Sponsor:

Takeda, visit bleedingdisorders.com to learn more.

It’s a Whole New World brought to you by @CSLBehring.

#bloodstreammedia #raredisease #bleedingdisorders #podcast #chronicdisease #genetherapy #healthcare #digitalhealth #biotech

Show Notes:

Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B

https://www.nejm.org/doi/full/10.1056/NEJMoa2514332

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